Fig 1. Diagram showing the main types of clinical study designs Treatment Studies Treatment studies aim to analyze the effect of an intervention such as a drug on a group of people. These types of ...

Natural history studies indicate that time-function tests are more responsive to treatment effect and more applicable to the 4–7 year old treatment group in DMD clinical studies, says McDonald.

Designing a study forces you to clarify your concepts and develop a goal. While challenging to consider all aspects of the process, the CRO can guide you, ensuring that you create a clinical study ...

A new study by investigators from Europe, including the Netherlands and the United Kingdom (UK), has shed light on ...

Let’s consider an example with a phase II clinical study in which 42% of the people receiving a new drug candidate for multiple myeloma experience the side effect of impaired vision.

SAN DIEGO, June 8, 2021 /PRNewswire/ -- Faro Health Inc., a cloud-computing company that simplifies the design and authoring of complex clinical studies for biopharma and medical device customers ...

The LUCE-1 clinical study is a first-in-human Phase 1/2 clinical study designed in collaboration with Prof. Simonelli and other leading experts in the field. Leveraging AAVantgarde’s proprietary ...

An Investigational New Drug (IND) is a drug or biological drug that has not been approved for general use by the FDA. It is used in a clinical trial to investigate its safety and efficacy.

Pfizer's presentation at the 2025 ASCO Annual Meeting will provide further insights into the trial design. Additional details on the study can be found at ClinicalTrials.gov (NCT06466187).

Dr. Toledano is the President of Biostatistics Consulting, LLC, which specializes in the design and analysis of clinical studies of medical imaging and in vitro diagnostic devices and works with ...

Though progress is being made in an indication with no known cure and only a handful of treatments, the recent wave of high-profile clinical studies in Duchenne muscular dystrophy (DMD) indicates ...