Sickle-cell is caused by inheriting two bad copies of one of the genes that make hemoglobin. Symptoms include bouts of intense pain, and life expectancy with the disease is just 53 years.

The US Food and Drug Administration on Friday approved two gene-based treatments for sickle cell disease, including the first therapy that uses the gene-editing technique CRISPR, opening a new era ...

The life-changing drug, developed by Boston-based Vertex and its Swiss partner CRISPR Therapeutics, targets sickle cell disease, an inherited blood disorder that causes crippling pain.

FDA approves first CRISPR therapy—here’s how it works against sickle cell The landmark treatment turns on another blood protein that prevents sickling. Beth Mole – Dec 8, 2023 6:27 pm | 75 ...

The UK’s regulator has approved the world’s first CRISPR–Cas9 gene editing therapy, which aims to cure sickle cell disease and transfusion-dependent β-thalassemia.

“One of my things I wanted was that for all the kids that sickle cell to get the metal ID bracelets and also for the adults, identified them with sickle cell. They should be made aware of that, ...

HACKENSACK, N.J. -- A New Jersey boy was cured of sickle cell anemia thanks to a medical breakthrough. Five-year-old Tobi Okunseinde from Haworth has a lot to thank his little brother Kwasi for ...

By comparison, research earlier this year showed medical expenses for current sickle cell treatments, from birth to age 65, add up to about $1.6 million for women and $1.7 million for men.

Those with sickle cell disease in the United States can have a shortened lifespan into their 50s, and even shorter in other countries. Roughly 100,000 Americans currently suffer from sickle cell ...