which is also known as Hurler or Hurler-Scheie syndrome. All three trials use ZFNs designed to edit liver cells at the same location in the albumin gene, but differ in delivering the corrective ...

MPS I, also known as Hurler, Scheie, or Hurler-Scheie syndrome, is a rare lysosomal storage disorder caused by the inability of the body’s cells to produce enough of an enzyme called alpha ...

Writing beautiful cursive is a challenge for everyone, and is even more difficult for Ezra due to Hurler Syndrome, an inherited metabolic disorder that the CDC says renders a person unable to ...

There are currently seven known different types of MPS disorders: MPS I (Hurler-Scheie syndrome), MPS II (Hunter syndrome), MPS III (Sanfilippo syndrome), MPS IV (Morquio syndrome), MPS VI ...