Bone marrow transplant offers a potential cure for thalassemia by replacing the faulty blood-forming stem cells with healthy ...

A Northeast Ohio woman and a 22-year-old man from UAE are among the first patients to receive the innovative CRISPR treatment.

That means it’s inherited or passed down from a parent to a child (or children). Sickle cell trait is different ... People with SCT have one normal hemoglobin gene (“A”) and one abnormal ...

“ Updated follow-up data of up to 10 years showed that patients treated with beti-cel in clinical trials experienced durable transfusion independence and normal or near-normal hemoglobin ...

MOST children with acquired aplastic anemia have increased concentrations of fetal hemoglobin in their peripheral blood. 1,2 The reasons for the elevated fetal hemoglobin concentration in this ...