Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

A Seward fifth grader battling a rare disease known as MPS, or Hurler Syndrome, was honored by her classmates Thursday.

Limerick hurler Kyle Hayes appeared in court on Monday, where it was confirmed he is to carry out 180 hours of community service instead of spending three months in jail. However, the judge warned ...

One former member of the St. Louis Cardinals is available after being designated for assignment on Sunday. Former Cardinals pitcher Kyle Gibson signed a one-year deal with the Baltimore Orioles ...

Get Instant Summarized Text (Gist) Engineered ferritin protein cages with precisely arranged histidine residues act as efficient metal-free peroxidase catalysts, achieving up to 80-fold higher ...

Adhiraj Gaikwad, a two-year-old with two rare genetic disorders, received a bone marrow transplant in Mumbai to treat Mucopolysaccharidosis Type 1 (MP ...

"Our study is a first step in dramatically expanding our repertoire of effective and safe CRISPR-Cas9 enzymes. In our manuscript, we demonstrate the utility of these PAMmla-predicted enzymes to ...

The Seattle Mariners got solid injury news on multiple fronts on Saturday. First, Logan Gilbert, out with a Grade 1 flexor strain, threw a bullpen at Petco Park in San Diego, hitting 95 mph.

Limerick hurler Kyle Hayes has avoided jail after a judge deemed him suitable for community service. Hayes was back in court on Monday, less than 24 hours after he was named man of the match in ...