The Food and Drug Administration (FDA) has approved Xuriden (uridine triacetate; Wellstat Therapeutics) oral granules for the treatment of hereditary orotic aciduria, the first approved treatment ...

US regulators have approved Wellstat Therapeutics' uridine triacetate for the treatment of hereditary orotic aciduria (HOA), an ultra-orphan indication that has been reported in only 20 people ...

Today, the U.S. Food and Drug Administration approved Xuriden (uridine triacetate), the first FDA-approved treatment for patients with hereditary orotic aciduria. Hereditary orotic aciduria is a ...

US regulators have green-lighted Xuriden, the first therapy for patients with the ultra rare metabolic disorder hereditary orotic aciduria. US regulators have green-lighted Xuriden, the first therapy ...

Glutaric aciduria type 1: Causes, symptoms, and treatment Medically reviewed by Adam Bernstein, MD, ScD — Written by Louise Morales-Brown on October 20, 2023 Definition ...

To the Editor: Neven et al. (June 28 issue)1 discuss the use of bone marrow transplantation in the treatment of severe mevalonic aciduria. We provide additional evidence for the effective cure of ...