HYOGO, Japan I July 8, 2025 I JCR Pharmaceuticals Co., Ltd. (TSE 4552; “JCR”) today announced that it has entered into a license agreement with Alexion, ...

Approximately 60 percent of children born with MPS-I have the most severe subtype, MPS-IH, also called Hurler syndrome, and rarely live past the age of 10 when untreated.

Orchard Therapeutics Announces Last Patient Treated in Registrational Trial of OTL-203 for MPS-I Hurler Syndrome Provided by GlobeNewswire Jul 7, 2025, 4:00:11 AM ...

Cutting-edge gene editing technology could eradicate Down syndrome, according to Japanese scientists. Down syndrome, which causes a range of developmental differences and affects 1 in 700 newborns ...

“Restless legs syndrome is a neurological disorder that is characterized by a need to move that is oftentimes associated with an uncomfortable feeling,” said Dr. John Winkelman, chief of the ...

The Milwaukee Brewers opted to not bring back a starting pitcher from the last few years this past offseason. Colin Rea was a solid piece for Milwaukee over th ...

Worse yet, Down syndrome porn — both artificially generated and not — is available in dark crevices of the internet.

Social media accounts using AI to impersonate people with Down syndrome are spreading, CBS News analysis shows, garnering dollars and millions of views while exploiting real advocates.

MPS I, also known as Hurler, Scheie, or Hurler-Scheie syndrome, is a rare lysosomal storage disorder caused by the inability of the body’s cells to produce enough of an enzyme called alpha ...

Ezra Rupple won Nicholas Maxim award through the Zaner-Bloser National Handwriting Contest. The 10-year-old has Hurler Syndrome.

"Imposter syndrome thrives in isolation, convincing women that they alone are flawed," writes Shari Dunn.

The Milwaukee Brewers 2025 campaign is off to a rough start following the announcement of a hurler who will undergo surgery.